SIMPATHIC

SIMPATHIC: Accelerating drug repurposing for rare neurological, neurometabolic and neuromuscular disorders by exploiting SIMilarities in clinical and molecular PATHology... Drug repurposing can fill an important gap for rare disease patient groups with large unmet medical needs. In comparison to traditional drug development, drug repurposing reduces the time and costs for drug development, because safety data are mostly available. Yet, the road from initial discovery to regulatory approval and market authorization can be winding and long. We need to increase the efficiency of the drug repurposing pathway to provide broader access to new therapeutic modalities for larger groups of patients.